Amsterdam Molecular Therapeutics’ focus is on the field of human gene therapy. AMT’s research and clinical development program fills an unmet medical need for therapy of severe (orphan) inherited diseases in the following areas - metabolic disorders, ocular diseases, CNS and the peripheral nervous system. AMT also offers product development and GMP manufacturing services for viral vectors to companies and academic institutes. AMT products include AMT-O10, macular degeneration gene therapy, neural regeneration gene therapy etc.